New therapies for sickle cell disease

Insulin has been used to treat type 1 diabetes for more than a century but now there is a new treatment being rolled out on the NHS that can delay the onset of the disease for years. Alongside, screening is gathering pace, identifying those that could benefit. So, is this the beg ...  Show more

More than six years since the start of the Covid pandemic, it might feel like we're pretty over it, yet that's simply not the case for the millions of people who suffer from long Covid. But could there be hope on the horizon? A new clinical trial led by University College London ...  Show more

2023 ended with an exciting biotech breakthrough for sickle cell patients. A gene-editing therapy using the revolutionary CRISPR technology provides new hope and options for the nearly 100,000 Americans with sickle cell disease. In this episode, we talk with the company behind on ...  Show more

Scientists have developed a long-sought treatment — perhaps even a cure — for sickle cell anemia. But getting it to patients might be an even bigger challenge. This episode was produced by Miles Bryan, edited by Matt Collette, fact-checked by Laura Bullard and Victoria Dominguez, ...  Show more

With its potential to expand the horizons of what’s possible for patients, CRISPR is the new darling of biotech. Reaching an important milestone in 2023 with the FDA approval of a sickle cell treatment using CRISPR, the technology is poised to break new barriers for treating pati ...  Show more

Sickle cell disease experts Drs. Angela Ellison [PEM] and Kim Smith-Whitley [Heme] join host Dr. Bob Belfer as they discuss advances in the care of children with this disease.